Rare Diseases & Orphan Drugs:
15. Rare Diseases & Orphan Drugs:
Illuminating the path for underserved patients. This session explores the unique challenges and opportunities in developing treatments for rare diseases, navigating regulatory incentives, and fostering collaboration to bring hope to those affected by these conditions
15-1 Orphan drug design process
15-2 Clinical trial challenges in rare diseases
15-3 Patient advocacy and access
15-4 Therapeutic Innovations for Rare Diseases: Accelerating Development & Improving Patient Outcomes
15-5 Global Perspectives on Rare Disease Research and Drug Development